Wainua (eplontersen) granted first-ever regulatory approval in US

eAwazMedicine

London – AstraZeneca and Ionis’ Wainua (eplontersen) has been approved in the US for the treatment of the polyneuropathy of hereditary transthyretin-mediated amyloidosis in adults, commonly referred to as hATTR-PN or ATTRv-PN.1 Wainua is the only approved medicine for the treatment of ATTRv-PN that can be self-administered via an auto-injector.2-4 The approval by the US Food and Drug Administration (FDA) was based on …